Detailed clinical, physiological and pathological phenotyping can impact access to disease-modifying treatments in ATTR carriers
Diane Beauvais, Céline Labeyrie, Cécile Cauquil, Bruno Francou, Ludivine Eliahou, Adeline Not, Andoni Echaniz-Laguna, Clovis Adam, Michel S Slama, Anouar Benmalek, Luca Leonardi, François Rouzet, David Adams, Vincent Algalarrondo, Guillemette Beaudonnet
Journal of Neurology, Neurosurgery & Psychiatry Oct 2023, jnnp-2023-332180; DOI: 10.1136/jnnp-2023-332180